Clinical characteristics and genotypes in the ADVANCE baseline data set, a comprehensive cohort of US children and adolescents with Pompe disease
Priya S. Kishnani(Duke Medical Center), Si Houn Hahn(University of Washington), Kristina An Haack(Sanofi (France)), Yang Zhao(Sanofi (United States)), Michael J. Gambello(Emory University), Jennifer Goldstein(University of North Carolina at Chapel Hill), David W. Stockton(Baylor College of Medicine), Susan Sparks(Children's National), Loren Peña(Cincinnati Children's Hospital Medical Center), James B. Gibson, Nancy D. Leslie(University of Cincinnati), David Kronn(New York Medical College), Pranoot Tanpaiboon(Children's National), Richard E. Hillman(University of Missouri Health System), Raymond Wang(Children's Hospital of Orange County)
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