Toxicology and Pharmacology of an AAV Vector Expressing Codon-Optimized RPGR in RPGR-Deficient Rd9 Mice
Chunjuan Song(Applied Genetic Technologies (United States)), Guojie Ye(Applied Genetic Technologies (United States)), Ping Zhu, Kari B. Green(University of Florida), Thomas J. Conlon(Adelson Foundation), Savitri Mandapati(Applied Genetic Technologies (United States)), Cayrn Plummer(University of Florida), Mailin Van Hoosear(Applied Genetic Technologies (United States)), David R. Knop(Applied Genetic Technologies (United States)), Wen‐Tao Deng(University of Florida), Kirsten E. Coleman(University of Florida), Jeffrey D. Chulay(Research Triangle Park Foundation), William W. Hauswirth(University of Florida), Paulette M. Robinson(Applied Genetic Technologies (United States)), Mark S. Shearman(Editas Medicine (United States)), Peter Sonnentag(Covance (United States)), Adrian M. Timmers(Applied Genetic Technologies (United States)), Alok Sharma
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