The Natural History of Inherited Retinal Dystrophy Due to Biallelic Mutations in the RPE65 Gene
Daniel C. Chung(Penn Presbyterian Medical Center), Kathleen Z. Reape(George Washington University), Markus N. Preising(Justus-Liebig-Universität Gießen), Birgit Lorenz(Justus-Liebig-Universität Gießen), Michael Larsen(University of Copenhagen), Richard G. Weleber(Oregon Health & Science University), Juliana Maria Ferraz Sallum(Fundação de Apoio à Universidade Federal de São Paulo), Julie DiStefano‐Pappas(Westat (United States)), Sarah McCague(Children's Hospital of Philadelphia), Eric A. Pierce(Broad Institute), Paul Yang(Oregon Health & Science University), Katherine A. High(Spark Therapeutics (United States)), Mark E. Pennesi(University of Pennsylvania), Mette Bertelsen(Zealand University Hospital), Knut Stieger(Justus-Liebig-Universität Gießen), Emily Place(MACOM (United States)), Grace Schaefer(Spark Therapeutics (United States)), Christian P. Hamel(Inserm), Bart Leroy(Children's Hospital of Philadelphia), Emily Liu(University of Iowa), Okan U. Elci(Westat (United States)), Jennifer Wellman(Children's Hospital of Philadelphia)
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