An immune tolerance approach using transient low-dose methotrexate in the ERT-naïve setting of patients treated with a therapeutic protein: experience in infantile-onset Pompe disease
Zoheb B. Kazi(Duke Medical Center), Priya S. Kishnani(Duke Medical Center), Neerja Gupta(All India Institute of Medical Sciences), Sheela Nampoothiri(Amrita Institute of Medical Sciences and Research Centre), R. Bradley Troxler(University of Alabama at Birmingham), Ankit K. Desai(Duke Medical Center), William B. Rizzo, Alexandra Joseph(Sanofi (United States)), Sherry Langston(Ochsner Health System), Alison McVie‐Wylie, Reeval Segel(Shaare Zedek Medical Center), Crystal Sung, Dmitriy Niyazov(Ochsner Health System), Omar Abdul‐Rahman(Cornell University), Annette Feigenbaum(Hospital for Sick Children), Susan Richards(MRC Clinical Trials Unit at UCL), David Kronn(New York Medical College), M.G. Sabbadini(IRCCS Ospedale San Raffaele), Pranoot Tanpaiboon(Children's National), Katalin Scherer(University of Arizona), Seymour Packman(University of California, San Francisco)
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