Haploinsufficiency leads to neurodegeneration in C9ORF72 ALS/FTD human induced motor neurons

Yingxiao Shi(University of Southern California), Shao‐Yu Lin(University of Southern California), Kim A. Staats(University of Southern California), Yichen Li(University of Southern California), Wen-Hsuan Chang(University of Southern California), Shu-Ting Hung(University of Southern California), Eric Hendricks(University of Southern California), Gabriel Linares(University of Southern California), Yaoming Wang(University of Southern California), Esther Son(Stanford University), Xinmei Wen(Thomas Jefferson University), Kassandra Kisler(University of Southern California), Brent Wilkinson(University of Southern California), Louise Menendez(University of Southern California), Tohru Sugawara(University of Southern California), Phillip Woolwine(University of Southern California), Mickey Huang(University of Southern California), Michael Cowan(University of Southern California), Brandon Ge(University of Southern California), Nicole Koutsodendris(University of Southern California), Kaitlin P Sandor(University of Southern California), Jacob Komberg(University of Southern California), Vamshidhar R. Vangoor(University Medical Center Utrecht), Ketharini Senthilkumar(University Medical Center Utrecht), Valerie Hennes(University of Southern California), Carina Seah(University of Southern California), Amy R. Nelson(University of Southern California), Tze-Yuan Cheng(DRVision Technologies (United States)), Shih-Jong J Lee(DRVision Technologies (United States)), Paul R. August, Jason Chen, Nicholas Wisniewski, Victor Hanson-Smith, T. Grant Belgard, Alice Zhang, Marcelo P. Coba(University of Southern California), Chris Grunseich(National Institutes of Health), Michael E. Ward(National Institutes of Health), Leonard H. van den Berg(University Medical Center Utrecht), R. Jeroen Pasterkamp(University Medical Center Utrecht), Davide Trotti(Thomas Jefferson University), Berislav V. Zloković(University of Southern California), Justin K. Ichida(University of Southern California)
Nature Medicine
February 5, 2018
Cited by 587Open Access
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