Gene therapy with adeno-associated virus vector 5–human factor IX in adults with hemophilia B
Wolfgang Miesbach(Goethe University Frankfurt), Frank W.G. Leebeek, Peter Kampmann(Rigshospitalet), Robert Klamroth(Vivantes Klinikum), Christian Niels Meyer(UniQure (Netherlands)), Federica Cattaneo(Chiesi (Italy)), Roger E. G. Schutgens(Utrecht University), Marco J.D. Tangelder(UniQure (Netherlands)), Karina Meijer(University Medical Center Groningen), Joachim Schwäble(Carl von Ossietzky Universität Oldenburg), Halvard Bönig(Goethe University Frankfurt), Michiel Coppens(Amsterdam UMC Location University of Amsterdam), Erhard Seifried(Goethe University Frankfurt), Giancarlo Castaman(Azienda Ospedaliero-Universitaria Careggi)
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