Gene therapy with adeno-associated virus vector 5–human factor IX in adults with hemophilia B
Wolfgang Miesbach(Goethe University Frankfurt), Frank W.G. Leebeek(Erasmus MC), Peter Kampmann(Rigshospitalet), Robert Klamroth(Klinikum im Friedrichshain), Christian Niels Meyer(UniQure (Netherlands)), Federica Cattaneo(Chiesi (Italy)), Roger E. G. Schutgens(University Medical Center Utrecht), Marco J.D. Tangelder(UniQure (Netherlands)), Karina Meijer(University Medical Center Groningen), Joachim Schwäble(Goethe University Frankfurt), Halvard Bönig(Goethe University Frankfurt), Michiel Coppens(Pulmonary Hypertension Association), Erhard Seifried(German Red Cross), Giancarlo Castaman(Azienda Ospedaliero-Universitaria Careggi)
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