Safety of Intradiaphragmatic Delivery of Adeno-Associated Virus-Mediated Alpha-Glucosidase (rAAV1-CMV- <i>hGAA</i> ) Gene Therapy in Children Affected by Pompe Disease
Manuela Corti(University of Florida), Barry J. Byrne(University of Florida), Thomas J. Conlon(Adelson Foundation), David D. Fuller(Brenau University), Cristina Liberati(University of Florida), İbrahim Sacit Tuna(University of Florida), Barbara K. Smith(University of Florida), Kirsten E. Coleman(University of Florida), Roland W. Herzog(Heidelberg University), Lee Ann Lawson(University of Florida), Saleem Islam(University of Florida), Shelley Collins(University of Florida)
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