A multicenter, retrospective medical record review of X‐linked myotubular myopathy: The recensus study
Alan H. Beggs(Boston Children's Hospital), Suyash Prasad(Vital Therapies (United States)), Sabrina W. Yum(Children's Hospital of Philadelphia), Tmirah Haselkorn, Imelda Hughes(Manchester University NHS Foundation Trust), Michele Yang(Children's Hospital Colorado), S. de Chastonay(Boston Children's Hospital), Barry J. Byrne(University of Florida), Jennifer Simon(Statistics Collaborative), Emma S. James(Vital Therapies (United States)), Nancy L. Kuntz(Lurie Children's Hospital), Lindsay C. Swanson(Boston Children's Hospital), Zi‐Fan Yu(Johannes Gutenberg University Mainz)
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