Quantification of microdystrophin and correlation to circulating biomarkers
Kristy J. Brown(Children's National), Carl Morris(Sylvana Research), Michael W. Lawlor(Medical College of Wisconsin), Pablo González(Solidus Biosciences (United States)), Joel Schneider(Solidus Biosciences (United States)), Diane Golebiowski(University of Massachusetts Chan Medical School), Valeria Ricotti(Solidus Biosciences (United States))
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