Gene Therapy Prolongs Survival and Restores Function in Murine and Canine Models of Myotubular Myopathy
Martin K. Childers(University of Washington), Anna Buj‐Bello(Pediatrics and Genetics), Fulvio Mavilio(The San Raffaele Telethon Institute for Gene Therapy), David L. Mack(California Institute for Regenerative Medicine), Nathalie Danièle(Genethon (France)), Robert W. Grange(Virginia Tech), Michael W. Lawlor(Medical College of Wisconsin), Laetitia van Wittenberghe(Genethon (France)), Alban Vignaud(Genethon (France)), Romain Joubert(Genethon (France)), Karine Poulard(Genethon (France)), Caroline Hammer(Genethon (France)), Christelle Moal(Institut Génétique Nantes Atlantique), Mark E. Furth(Regeneron (United States)), Alan H. Beggs(Boston Children's Hospital), Christel Rivière(Genethon (France)), Branden E. Rider(Boston Children's Hospital), Melissa Goddard(Forest Institute), Mandy Lockard(Forest Institute), Carole Masurier(Genethon (France)), Samia Martin(Genethon (France)), Xuan Guan(Forest Institute), Erin Mitchell(Forest Institute), T. Soker(Children's Hospital of Wisconsin), Jonathan Doering(Cape Breton University), Jane Barber(Forest Institute), Thibaud Jamet(Genethon (France)), J. Koudy Williams(Forest Institute), Philippe Moullier(Inserm)
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