Long‐term effects of systemic gene therapy in a canine model of myotubular myopathy
Matthew Elverman(University of Washington), Martin K. Childers(University of Washington), Robert W. Grange(Virginia Tech), Michael W. Lawlor(Medical College of Wisconsin), Valerie E. Kelly(University of Washington), Karine Poulard(Genethon (France)), Hui Meng(Medical College of Wisconsin), Alan H. Beggs(Boston Children's Hospital), Jessica M. Snyder(University of Washington), Melissa Goddard(Forest Institute), Anthony P. Marsh(Wake Forest University), A. Buj-Bello(Inserm), David L. Mack(California Institute for Regenerative Medicine)
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