Systemic AAV8-Mediated Gene Therapy Drives Whole-Body Correction of Myotubular Myopathy in Dogs
David L. Mack(California Institute for Regenerative Medicine), Martin K. Childers(University of Washington), Fulvio Mavilio(The San Raffaele Telethon Institute for Gene Therapy), M. W. O'CALLAGHAN, Matthew Elverman(University of Washington), Robert W. Grange(Virginia Tech), Michael W. Lawlor(Medical College of Wisconsin), Virginie Latournerie(Inserm), Valerie E. Kelly(University of Washington), Karine Poulard(Genethon (France)), Annie G. Brezovec(Virginia Tech), Federico Mingozzi(Inserm), Laurine Buscara(Inserm), Hui Meng(Medical College of Wisconsin), Alan H. Beggs(Boston Children's Hospital), Barbara K. Smith(University of Florida), Nikhil Gopal(University of Washington), Jessica M. Snyder(University of Washington), Melissa Goddard(Forest Institute), P. Véron(Genethon (France)), Jennifer L. Strande(Amgen (United States)), Ana Buj‐Bello(Inserm), Fujun Liu(University of Florida), Lin Yang(Northwest University), Jérôme Denard(Genethon (France)), Christine Le Bec(Genethon (France)), Jean‐Yves Hogrel(Institut de Myologie)
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