Gain of Toxicity from ALS/FTD-Linked Repeat Expansions in C9ORF72 Is Alleviated by Antisense Oligonucleotides Targeting GGGGCC-Containing RNAs
Jie Jiang(University of California San Diego), Qiang Zhu(University of California San Diego), Tania F. Gendron(Mayo Clinic in Florida), Shahram Saberi(University of California San Diego), Melissa McAlonis‐Downes(University of California San Diego), Amanda Seelman(University of California San Diego), Jennifer E. Stauffer(University of California San Diego), Paymaan Jafar‐Nejad(Ionis Pharmaceuticals (United States)), Kevin Drenner(University of California San Diego), Derek Schulte(University of California San Diego), Seung Chun(Ionis Pharmaceuticals (United States)), Shuying Sun(University of California San Diego), Shuo‐Chien Ling(National University of Singapore), Brian Myers(University of California San Diego), Jeffery A. Engelhardt(Ionis Pharmaceuticals (United States)), Melanie Katz(Ionis Pharmaceuticals (United States)), Michael W. Baughn(University of California San Diego), Oleksandr Platoshyn(University of California San Diego), Martin Maršala(Slovak Academy of Sciences), Andy Watt(Ionis Pharmaceuticals (United States)), Charles J. Heyser(University of California San Diego), M. Colin Ard(University of California San Diego), Louis De Muynck(VIB-KU Leuven Center for Brain & Disease Research), Lillian M. Daughrity(Mayo Clinic in Florida), Deborah A. Swing(National Cancer Institute), Lino Tessarollo(National Cancer Institute), Chris Jung, Arnaud Delpoux(University of California San Diego), Daniel T. Utzschneider(University of California San Diego), Stephen Μ. Hedrick(University of California San Diego), Pieter J. de Jong, Dieter Edbauer(German Center for Neurodegenerative Diseases), Philip Van Damme(VIB-KU Leuven Center for Brain & Disease Research), Leonard Petrucelli(Mayo Clinic in Florida), Christopher E. Shaw(King's College London), C. Frank Bennett(Ionis Pharmaceuticals (United States)), Sandrine Da Cruz(University of California San Diego), John Ravits(University of California San Diego), Frank Rigo(Ionis Pharmaceuticals (United States)), Don W. Cleveland(University of California San Diego), Clotilde Lagier‐Tourenne(University of California San Diego)
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