Sustained Therapeutic Reversal of Huntington's Disease by Transient Repression of Huntingtin Synthesis
Holly Kordasiewicz(University of California San Diego), Lisa M. Stanek, Edward V. Wancewicz(Ionis Pharmaceuticals (United States)), Curt Mazur(Ionis Pharmaceuticals (United States)), Melissa McAlonis(University of California San Diego), Kimberly A. Pytel(University of California San Diego), Jonathan W. Artates(University of California San Diego), Andreas Weiss(Novartis (Switzerland)), Seng H. Cheng, Lamya S. Shihabuddin, Gene Hung(Ionis Pharmaceuticals (United States)), C. Frank Bennett(Ionis Pharmaceuticals (United States)), Don W. Cleveland(University of California San Diego)
Cited by 765Open Access