Clinical Evaluation of a Recombinant Adeno-Associated Virus (rAAV) Alpha-1 Antitrypsin (AAT) Gene Therapy Vector.
Jeff Chulay, Terence R. Flotte(University of Massachusetts Chan Medical School), Christopher R. Mueller(Queen's University), James M. Wilson(St Bartholomew's Hospital), Mark Brantly(University of Florida), L Wang, L. Terry Spencer(University of Florida), Margaret Humphries(University of Massachusetts Chan Medical School), Barry J. Byrne(University of Florida), Cheryl Spencer, Farshid N. Rouhani(University of Florida), Thomas J. Conlon(Adelson Foundation)
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