Time to treatment benefit for adult patients with Fabry disease receiving agalsidase β: data from the Fabry Registry

Alberto Ortíz(Fundación Renal), David G. Warnock(University of Alabama at Birmingham), Manesh R. Patel(Clinical Research Institute), Robert J. Hopkin(Cincinnati Children's Hospital Medical Center), João Paulo Oliveira(Universidade do Porto), Christoph Wanner(University of Würzburg), Ana Jovanović(Manchester Academic Health Science Centre), Dominique P. Germain(Université de Versailles Saint-Quentin-en-Yvelines), Aleš Linhart(Charles University), Ademola K. Abiose(Ohio Heart & Vascular Center), Gustavo Cabrera, Juan Politei(Ofcom), Daniel G. Bichet(Hôpital du Sacré-Cœur de Montréal), Stephen Waldek, Sonia S. Maruti, Michael Mauer(University of Minnesota), Joel Charrow(Northwestern University), Han‐Wook Yoo(CHA University Bundang Medical Center)
Journal of Medical Genetics
March 18, 2016
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