Time to treatment benefit for adult patients with Fabry disease receiving agalsidase β: data from the Fabry Registry

Alberto Ortíz(Universidad Pontificia de Salamanca), David G. Warnock(University of Alabama at Birmingham), Manesh R. Patel(Duke University), Robert J. Hopkin(Cincinnati Children's Hospital Medical Center), João Paulo Oliveira(Universidade do Porto), Christoph Wanner(Universitätsklinikum Würzburg), Ana Jovanović(Manchester Academic Health Science Centre), Dominique P. Germain(Assistance Publique – Hôpitaux de Paris), Aleš Linhart(Charles University), Ademola K. Abiose(Ohio Heart & Vascular Center), Gustavo Cabrera, Juan Politei(Development Fund), Daniel G. Bichet(Hôpital du Sacré-Cœur de Montréal), Stephen Waldek, Sonia S. Maruti, Michael Mauer(University of Minnesota), Joel Charrow(Northwestern University), Han‐Wook Yoo(CHA University Bundang Medical Center)
Journal of Medical Genetics
March 18, 2016
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