AAV Gene Therapy Strategies for Lysosomal Storage Disorders with Central Nervous System Involvement
Diane Golebiowski(University of Massachusetts Chan Medical School), Miguel Sena‐Esteves(University of Massachusetts Chan Medical School), Wael F. Asaad(Allen Institute for Brain Science), J. L. Sartin(Auburn University), Lorelei Stoica(University of Massachusetts Chan Medical School), Allison M. Bradbury(Nationwide Children's Hospital), Douglas R. Martin(Auburn University), Brian K Whitlock(Knoxville College), Anna Luisa Kühn(University of Massachusetts Chan Medical School), Diane U. Wilson(Auburn University), Aime K. Johnson(Auburn University), Churl‐Su Kwon(Columbia University Irving Medical Center), Heather Gray‐Edwards(UMass Memorial Health Care), Judith A. Hudson(Cambridge University Press), Ashley N. Randle(Auburn University), Matthew J. Gounis(University of Massachusetts Chan Medical School), Jacob A. Johnson(Auburn University), I.M.J. van der Bom(University of Massachusetts Chan Medical School)
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