Direct Intracranial Injection of AAVrh8 Encoding Monkey β-N-Acetylhexosaminidase Causes Neurotoxicity in the Primate BrainDiane Golebiowski, Miguel Sena‐Esteves, Keiko Y. Petrosky et al.|Human Gene Therapy|2017Cited by 93
AAV Gene Therapy Strategies for Lysosomal Storage Disorders with Central Nervous System InvolvementDiane Golebiowski, Miguel Sena‐Esteves, Allison M. Bradbury et al.|Neuromethods|2015Cited by 6