Clinical characteristics and genotypes in the ADVANCE baseline dataset, a comprehensive cohort of us children and youth with Pompe disease
Priya S. Kishnani(Duke Medical Center), Sihoun Hahn(Mayo Clinic), Raymond Wang(Children's Hospital of Orange County), Kristina An Haack(Sanofi (France)), Yang Zhao(Sanofi (United States)), Michael J. Gambello(Emory University), David W. Stockton(Baylor College of Medicine), Susan Sparks(Children's National), Loren Peña(Cincinnati Children's Hospital Medical Center), James B. Gibson, Nancy Leslie(Cincinnati Children's Hospital Medical Center), David Kronn(New York Medical College), Richard E. Hillman(University of Missouri Health System), Pranoot Tanpaiboon(Children's National)
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