Enzyme replacement therapy rescues weakness and improves muscle pathology in mice with X-linked myotubular myopathy
Michael W. Lawlor(Medical College of Wisconsin), Alan H. Beggs(Boston Children's Hospital), M. W. O'CALLAGHAN, Jeffrey J. Widrick(University of Massachusetts Chan Medical School), Robert W. Grange(Virginia Tech), Marissa G. Viola(Boston Children's Hospital), Hui Meng(Medical College of Wisconsin), Christopher R. Pierson(Nationwide Children's Hospital), Cynthia P. Hsu(Boston Children's Hospital), Martin K. Childers(University of Washington), Anna Buj‐Bello(Pediatrics and Genetics), Dustin Armstrong
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