Mucopolysaccharidosis type IIIA: Clinical spectrum and genotype‐phenotype correlations
M. J. Valstar(Amsterdam UMC Location University of Amsterdam), Frits A. Wijburg(Emma Kinderziekenhuis), Dicky Halley(Norwegian Institute for Nature Research), Sanne Neijs(Erasmus MC), George J. G. Ruijter(Wageningen University & Research), Ron A. Wevers(Radboud University Nijmegen), Hennie T. Brüggenwirth(Erasmus MC), Ben J. H. M. Poorthuis(Amsterdam UMC Location University of Amsterdam), Otto P. van Diggelen(Erasmus MC), Renske Olmer(Erasmus MC)
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