Mucopolysaccharidosis type IIIA: Clinical spectrum and genotype‐phenotype correlations
M. J. Valstar(Amsterdam UMC Location University of Amsterdam), Frits A. Wijburg(Emma Kinderziekenhuis), Dicky Halley(Erasmus University Rotterdam), Sanne Neijs(Erasmus MC), George J. G. Ruijter(Wageningen University & Research), Ron A. Wevers(Radboud University Medical Center), Hennie T. Brüggenwirth(Erasmus MC), Ben J. H. M. Poorthuis(Amsterdam UMC Location University of Amsterdam), Otto P. van Diggelen(Erasmus MC), Renske Olmer(Erasmus MC)
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