Recommendations for the diagnosis and management of Niemann–Pick disease type C: An update
Marc C. Patterson(Mayo Clinic in Florida), Christian J. Hendriksz(Birmingham Children's Hospital), Mark Walterfang(The Royal Melbourne Hospital), Frédéric Sedel(Sorbonne Université), Marie T. Vanier(Inserm), Frits A. Wijburg(Academic Medical Center)
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