Single-Stranded RNAs Use RNAi to Potently and Allele-Selectively Inhibit Mutant Huntingtin Expression

Dongbo Yu(Southwestern Medical Center), Hannah M. Pendergraff(Southwestern Medical Center), Jing Liu(Southwestern Medical Center), Holly Kordasiewicz(Ionis Pharmaceuticals (United States)), Don W. Cleveland(University of California San Diego), Eric E. Swayze(Ionis Pharmaceuticals (United States)), Walt F. Lima(Ionis Pharmaceuticals (United States)), Stanley T. Crooke(Ionis Pharmaceuticals (United States)), Thazha P. Prakash(Ionis Pharmaceuticals (United States)), David R. Corey(Southwestern Medical Center)
Cell
August 1, 2012
10.1016/j.cell.2012.08.002
Cited by 275Open Access
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Abstract

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