Self-reported treatment-associated symptoms among patients with urea cycle disorders participating in glycerol phenylbutyrate clinical trials
Sandesh C.S. Nagamani(Baylor College of Medicine), Masoud Mokhtarani, Cary O. Harding(Oregon Health & Science University), Andreas Schulze(University of Toronto), Klara Dickinson, George A. Díaz(Icahn School of Medicine at Mount Sinai), Dion F. Coakley, J. Lawrence Merritt(University of Washington), Jerry Vockley(Pittsburgh Public Schools), Derek A. Wong(University of California, Los Angeles), William Berquist(Palo Alto University), Mark Korson(Tufts Medical Center), Wendy E. Smith(Maine Medical Center), Bruce F. Scharschmidt, Cynthia Le Mons(National Urea Cycle Disorders Foundation), Dennis Bartholomew(Nationwide Children's Hospital), Uta Lichter‐Konecki(Children's National), Miguel Marino(Tufts Medical Center), Nicola Longo(Center for Human Genetics), Brendan H. Lee(Baylor College of Medicine), Annette Feigenbaum(Hospital for Sick Children), Shawn E. McCandless(University Hospitals of Cleveland), Robert Zori(University of Florida), David Kronn(New York Medical College), James Bartley(MemorialCare Long Beach Medical Center), Renata C. Gallagher(Children's Hospital Colorado), Susan A. Berry(University of Minnesota), Stephen Cederbaum(University of California, Los Angeles), William J. Rhead(Children's Hospital of Wisconsin)
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