In Utero Gene Therapy Rescues Vision in a Murine Model of Congenital Blindness
Nadine S. Dejneka(Penn Presbyterian Medical Center), Jean Bennett(Penn Presbyterian Medical Center), Arkady Lyubarsky(Penn Presbyterian Medical Center), T. Michael Redmond(National Institutes of Health), Artur V. Cideciyan(University of Pennsylvania), Tonia S. Rex(Vanderbilt University Medical Center), Ernest Glover(Penn Presbyterian Medical Center), Edward N. Pugh(Membrane Technology & Research (United States)), Samuel G. Jacobson(Penn Presbyterian Medical Center), Albert M. Maguire(Children's Hospital of Philadelphia), Enrico Maria Surace(Telethon Institute Of Genetics And Medicine), Zhangyong Wei(Penn Presbyterian Medical Center), Tomás S. Alemán(Children's Hospital of Philadelphia), Waixing Tang(Penn Presbyterian Medical Center), A. Savchenko(Russian Federal Space Agency)
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