Early access experience with VPRIV®: Recommendations for ‘core data’ collection
Derralynn Hughes(Royal Free London NHS Foundation Trust), Neal J. Weinreb, Ian J. Cohen(Rabin Medical Center), Gregory M. Pastores(New York University), Maciej Machaczka(Karolinska University Hospital), Chaim Kaplinsky(Tel Aviv University), Tobias Böttcher(Institut für Schlaganfall- und Demenzforschung), Nadia Belmatoug(Hôpital Beaujon), Terence Eagleton(Takeda (United States)), Ari Zimran(Hebrew University of Jerusalem), Allan M. Lund(Copenhagen University Hospital), Hanna Rosenbaum(University of Namur), Simon Jones(New York University), Maria Domenica Cappellini(Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico), Eugen Mengel(University of Hohenheim), Pilar Giraldo(Université Paris-Saclay), Nikolaus Tiling(Charité - Universitätsmedizin Berlin), Olaf A. Bodamer(Broad Institute), Deborah Elstein(Shaare Zedek Medical Center), Panagiotis Tsaftaridis(Laiko General Hospital of Athens), Moeen Al-Sayed(King Faisal Specialist Hospital & Research Centre), Malvin Sjo(Haukeland University Hospital)
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