Recommendations for initiation and cessation of enzyme replacement therapy in patients with Fabry disease: the European Fabry Working Group consensus document

Marieke Biegstraaten(Amsterdam UMC Location University of Amsterdam), Carla E. M. Hollak(Amsterdam UMC Location University of Amsterdam), Frank Weidemann(Katharinenhospital), Patrick Deegan(Addenbrooke's Hospital), Gabor E. Linthorst(Amsterdam UMC Location University of Amsterdam), Claudia Sommer(University of North Carolina at Chapel Hill), Ilkka Kantola(Turku University Hospital), Derralynn Hughes(Royal Free London NHS Foundation Trust), João Paulo Oliveira(Universidade do Porto), Wim Terryn(Ghent University Hospital), Atul Mehta(National Health Service), Einar Svarstad(Haukeland University Hospital), Uma Ramaswami(The Royal Free Hospital), Gere Sunder–Plassmann(Medical University of Vienna), Annelies Sweeb(University of Twente), Frits A. Wijburg(Emma Kinderziekenhuis), Tarekegn Geberhiwot(Selly Oak Hospital), Frédéric Barbey(University Hospital of Lausanne), Anna Tylki‐Szymańska(Children's Memorial Health Institute), Camilla Tøndel(Haukeland University Hospital), Nesrin Karabul(German Center for Pediatric and Adolescent Rheumatology), Bojan Vujkovac(Šolski center Slovenj Gradec), Dominique P. Germain(Université de Versailles Saint-Quentin-en-Yvelines), Peter Woolfson(Salford Royal NHS Foundation Trust), Christian J. Hendriksz(Birmingham Children's Hospital), Rossella Parini(Azienda Ospedaliera San Gerardo), Reynir Arngrı́msson(University of Iceland), Ulla Feldt‐Rasmussen(Copenhagen University Hospital), Andreas L. Serra(University of Zurich), Erica van de Mheen(Vector Fabrics (Netherlands)), Franco Cecchi(Azienda Ospedaliero-Universitaria Careggi), Christine Lavery(Amersham Hospital), Michael Rudnicki(Innsbruck Medical University), Lut Boks(Amersham Hospital)
Orphanet Journal of Rare Diseases
March 27, 2015
Cited by 345


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