881. Safety, Efficacy and Biodistribution of Recombinant AAV2-RPE65 Vector Delivered by Ocular Subretinal Injection
Samuel G. Jacobson(Penn Presbyterian Medical Center), William W. Hauswirth(University of Florida), Tomás S. Alemán(Children's Hospital of Philadelphia), Thomas J. Conlon(Adelson Foundation), Geoffrey K. Aguirre(University of Pennsylvania), Caroline J. Zeiss(Yale University), Artur V. Cideciyan(University of Pennsylvania), András M. Komáromy(University of Pennsylvania), Jean Bennett(Penn Presbyterian Medical Center), Alejandro J. Román(Penn Presbyterian Medical Center), Elizabeth A. M. Windsor(Penn Presbyterian Medical Center), Alexander Sumaroka(Penn Presbyterian Medical Center), Susan E. Pearce-Kelling(Cornell University), Quihong Li, Gregory M. Acland(Cornell University), Albert M. Maguire(Children's Hospital of Philadelphia), Sharon Schwartz(Penn Presbyterian Medical Center), Sanford L. Boye(University of Florida), Vincent A. Chiodo(University of Florida), Terence R. Flotte(University of Massachusetts Chan Medical School)
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