Safety of Recombinant Adeno-Associated Virus Type 2–RPE65 Vector Delivered by Ocular Subretinal Injection

Samuel G. Jacobson(Penn Presbyterian Medical Center), William W. Hauswirth(University of Florida), Tomás S. Alemán(Children's Hospital of Philadelphia), Thomas J. Conlon(Adelson Foundation), Geoffrey K. Aguirre(University of Pennsylvania), Caroline J. Zeiss(Yale University), Artur V. Cideciyan(University of Pennsylvania), András M. Komáromy(University of Pennsylvania), Jean Bennett(Penn Presbyterian Medical Center), Alejandro J. Román(Penn Presbyterian Medical Center), Elizabeth A. M. Windsor(Penn Presbyterian Medical Center), Alexander Sumaroka(Penn Presbyterian Medical Center), Susan E. Pearce-Kelling(Cornell University), Gregory M. Acland(Cornell University), Albert M. Maguire(Children's Hospital of Philadelphia), Sharon Schwartz(Penn Presbyterian Medical Center), Shalesh Kaushal(University of Florida), Sanford L. Boye(University of Florida), Vincent A. Chiodo(University of Florida), Terence R. Flotte(University of Massachusetts Chan Medical School)
Molecular Therapy
May 3, 2006
Cited by 223


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