Elevated plasma glucosylsphingosine in Gaucher disease: relation to phenotype, storage cell markers, and therapeutic response
Nick Dekker(Amsterdam UMC Location University of Amsterdam), Johannes M. F. G. Aerts(Leiden University Medical Center), Saskia Scheij(Amsterdam UMC Location University of Amsterdam), J.E.M. Groener(Amsterdam UMC Location University of Amsterdam), Maria J. Ferraz(Amsterdam UMC Location University of Amsterdam), Frits A. Wijburg(Emma Kinderziekenhuis), Mario Maas(Amsterdam UMC Location University of Amsterdam), Laura van Dussen(Amsterdam UMC Location University of Amsterdam), Anna Tylki‐Szymańska(Children's Memorial Health Institute), Mariëlle J. van Breemen(Amsterdam UMC Location University of Amsterdam), Pramod K. Mistry(Yale University), Herman S. Overkleeft(Leiden University), Dave Speijer(Amsterdam University Medical Centers), Rolf G. Boot(Leiden University), Karen Ghauharali(Amsterdam UMC Location University of Amsterdam), Carla E. M. Hollak(Centre For Development Studies)
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