Correction of Dystrophin Expression in Cells From Duchenne Muscular Dystrophy Patients Through Genomic Excision of Exon 51 by Zinc Finger Nucleases
David G. Ousterout(Profectus Biosciences (United States)), Charles A. Gersbach(Duke University), Ami M. Kabadi(Sarepta Therapeutics (United States)), Pratiksha I. Thakore(Broad Institute), Matthew T. Brown(Emory University), Pablo Pérez‐Piñera(University of Illinois Urbana-Champaign), William H. Majoros(Duke University), Timothy E. Reddy(Duke University)
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