Phase 2 comparison of a novel ammonia scavenging agent with sodium phenylbutyrate in patients with urea cycle disorders: Safety, pharmacokinetics and ammonia control
Brendan Lee(Baylor College of Medicine), Klara Dickinson, Jean‐Francois Marier(Princeton University), Martin Béliveau, Joseph Mauney, Bruce F. Scharschmidt, Asad Mian(Baylor College of Medicine), William J. Rhead(Children's Hospital of Wisconsin), Oleg A. Shchelochkov(Baylor College of Medicine), George A. Díaz(Icahn School of Medicine at Mount Sinai)
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