Successful immune tolerance induction to enzyme replacement therapy in CRIM-negative infantile Pompe disease
Yoav H. Messinger(Children’s Minnesota - St. Paul Hospital), Priya S. Kishnani(Duke Medical Center), Cara Wells(Children's Hospital of Wisconsin), Nancy J. Mendelsohn, Eli Hershkovitz(Soroka Medical Center), Rebecca Olson(Children’s Minnesota - St. Paul Hospital), Simon Jones(Manchester University NHS Foundation Trust), Amy White, Deeksha Bali(MRC Epidemiology Unit), Laura E. Case, Michael Champion, Sarah P. Young(Duke Medical Center), William J. Rhead(Children's Hospital of Wisconsin), Amy S. Rosenberg(Center for Drug Evaluation and Research), David Dimmock(Children’s Institute)
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