Multiplex CRISPR/Cas9-based genome editing for correction of dystrophin mutations that cause Duchenne muscular dystrophy
David G. Ousterout(Profectus Biosciences (United States)), Charles A. Gersbach(Duke University), Timothy E. Reddy(Duke University), Ami M. Kabadi(Sarepta Therapeutics (United States)), Pratiksha I. Thakore(Broad Institute), William H. Majoros(Duke University)
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