Functional Repair of CFTR by CRISPR/Cas9 in Intestinal Stem Cell Organoids of Cystic Fibrosis Patients

Gerald Schwank(University Medical Center Utrecht), Bon‐Kyoung Koo(University Medical Center Utrecht), Valentina Sasselli(University Medical Center Utrecht), Johanna F. Dekkers(Wilhelmina Children's Hospital), Inha Heo(University Medical Center Utrecht), Turan Demircan(Hubrecht Institute for Developmental Biology and Stem Cell Research), Nobuo Sasaki(University Medical Center Utrecht), Sander Boymans(Hubrecht Institute for Developmental Biology and Stem Cell Research), Edwin Cuppen(University Medical Center Utrecht), Cornelis K. van der Ent(Wilhelmina Children's Hospital), Edward E. S. Nieuwenhuis(Wilhelmina Children's Hospital), Jeffrey M. Beekman(University Medical Center Utrecht), Hans Clevers(University Medical Center Utrecht)
Cell stem cell
December 1, 2013
10.1016/j.stem.2013.11.002
Cited by 1,393Open Access
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