Safety in Nonhuman Primates of Ocular AAV2- <i>RPE65</i> , a Candidate Treatment for Blindness in Leber Congenital Amaurosis
Samuel G. Jacobson(Penn Presbyterian Medical Center), William W. Hauswirth(University of Florida), Tomás S. Alemán(Children's Hospital of Philadelphia), Thomas J. Conlon(Adelson Foundation), Geoffrey K. Aguirre(University of Pennsylvania), Caroline J. Zeiss(Yale University), Artur V. Cideciyan(University of Pennsylvania), András M. Komáromy(University of Pennsylvania), Michelle Doobrajh(Penn Presbyterian Medical Center), Alejandro J. Román(Penn Presbyterian Medical Center), Alexander Sumaroka(Penn Presbyterian Medical Center), Susan E. Pearce-Kelling(Cornell University), Albert M. Maguire(Children's Hospital of Philadelphia), Sharon Schwartz(Penn Presbyterian Medical Center), Shalesh Kaushal(University of Florida), Sanford L. Boye(University of Florida), Andy Y. Cheung(Penn Presbyterian Medical Center), Terence R. Flotte(University of Massachusetts Chan Medical School)
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