One year outcomes of diaphragm gene therapy in ventilator dependent children with Pompe disease
Barry J. Byrne(University of Florida), Shelley Collins(University of Florida), Thomas J. Conlon(Adelson Foundation), Barbara K. Smith(University of Florida), Dawn Phillips(ProterixBio (United States)), Lee Ann Lawson(University of Florida), Daniel B. Martin(King's College London), Cathryn Mah(Anna Needs Neuroblastoma Answers)
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