Phase I/II Trial of Diaphragm Delivery of Recombinant Adeno-Associated Virus Acid Alpha-Glucosidase (rAAV1-CMV- <i>GAA</i> ) Gene Vector in Patients with Pompe Disease
Barry J. Byrne(University of Florida), Shelley Collins(University of Florida), Manuela Corti(University of Florida), Cathryn Mah(Anna Needs Neuroblastoma Answers), Thomas J. Conlon(Adelson Foundation), Nicole Dobija(University of Florida), Daniel Martı́n(National Institutes of Health), Brian Cleaver(University of Florida), Maria V. Irwin(University of Florida), Barbara K. Smith(University of Florida), Lee Ann Lawson(University of Florida), Saleem Islam(University of Florida), Nathalie Clément(University of Florida)
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