Phase I/II Trial of Diaphragm Delivery of Recombinant Adeno-Associated Virus Acid Alpha-Glucosidase (rAAV1-CMV- <i>GAA</i> ) Gene Vector in Patients with Pompe DiseaseBarry J. Byrne, Shelley Collins, Cathryn Mah et al.|Human Gene Therapy Clinical Development|2014Cited by 45