Allele-Selective Inhibition of Mutant Huntingtin with 2-Thio- and C5- Triazolylphenyl-Deoxythymidine-Modified Antisense Oligonucleotides
Michael E. Østergaard(Ionis Pharmaceuticals (United States)), Punit P. Seth(Ionis Pharmaceuticals (United States)), Andrew T. Watt(University of British Columbia), Poul Nielsen(University of Southern Denmark), Pawan Kumar(Kurukshetra University), Josh G. Nichols(Ionis Pharmaceuticals (United States)), Pawan K. Sharma(Kurukshetra University)
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