Fatty acid conjugation enhances potency of antisense oligonucleotides in muscle

Thazha P. Prakash(Ionis Pharmaceuticals (United States)), Punit P. Seth(Ionis Pharmaceuticals (United States)), Adam E. Mullick(Ionis Pharmaceuticals (United States)), Michael E. Østergaard(Ionis Pharmaceuticals (United States)), Audrey Low(Ionis Pharmaceuticals (United States)), Sue Murray(Ionis Pharmaceuticals (United States)), Alfred E. Chappell(Ionis Pharmaceuticals (United States)), Jinghua Yu(Albert Einstein College of Medicine), Richard Lee(Ionis Pharmaceuticals (United States)), Eric E. Swayze(Ionis Pharmaceuticals (United States)), Steve T. Yeh(Ionis Pharmaceuticals (United States)), Hans Gaus(Ionis Pharmaceuticals (United States))
Nucleic Acids Research
April 26, 2019
Cited by 151


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