ASO-Based PKM Splice-Switching Therapy Inhibits Hepatocellular Carcinoma GrowthWai Kit, Adrian R. Krainer|Cancer Research|2021Cited by 116
Splicing Factor SRSF1 Promotes Pancreatitis and KRASG12D-Mediated Pancreatic CancerLedong Wan, Adrian R. Krainer|Cancer Discovery|2023Cited by 65
Gene-specific nonsense-mediated mRNA decay targeting for cystic fibrosis therapyYoung Jin Kim, Adrian R. Krainer|Nature Communications|2022Cited by 40
Antisense oligonucleotide therapy for H3.3K27M diffuse midline gliomaQian Zhang, Adrian R. Krainer|Science Translational Medicine|2023Cited by 28
PKM splice-switching ASOs induce upregulation of dual-specificity phosphatases and dephosphorylation of ERK1/2 in hepatocellular carcinomaDillon M. Voss, Adrian R. Krainer|Journal of Biological Chemistry|2025Cited by 6