Multidisciplinary Management of Hunter SyndromeJoseph Muenzer, Ed Wraith, Michael Beck et al.|PEDIATRICS|2009Cited by 193
Allogeneic hematopoietic SCT for alpha-mannosidosis: an analysis of 17 patientsMartin Mynarek, K-W Sykora, David A. Jacobsohn et al.|Bone Marrow Transplantation|2011Cited by 92
Consensus guidelines for the monitoring and management of metachromatic leukodystrophy in the United StatesLaura Adang, Adeline Vanderver, Joshua L. Bonkowsky et al.|Cytotherapy|2024Cited by 25
Improved Brain Pathology and Progressive Peripheral Neuropathy in a 15 Year Old Survivor of Infantile Krabbe Disease Treated With Umbilical Cord TransplantationJulia Kofler, Maria L. Escolar|Frontiers in Molecular Neuroscience|2022Cited by 9