CRISPR-Cas9-Mediated Genome Editing Increases Lifespan and Improves Motor Deficits in a Huntington’s Disease Mouse ModelFreja K. Ekman, Thomas Gaj|Molecular Therapy — Nucleic Acids|2019Cited by 153
CRISPR base editing of <i>cis</i> -regulatory elements enables target gene perturbationsColin K.W. Lim, Thomas Gaj|bioRxiv (Cold Spring Harbor Laboratory)|2022Cited by 0