Regulating PCCA gene expression by modulation of pseudoexon splicing patterns to rescue enzyme activity in propionic acidemiaUlrika Simone Spangsberg Petersen, Brage Storstein Andresen|Molecular Therapy — Nucleic Acids|2023Cited by 16
Regulating <i>PCCA</i> gene expression by modulation of pseudoexon splicing patterns to rescue enzyme activity in propionic acidemiaUlrika Simone Spangsberg Petersen, Brage Storstein Andresen|bioRxiv (Cold Spring Harbor Laboratory)|2023Cited by 0