Whole body correction of mucopolysaccharidosis IIIA by intracerebrospinal fluid gene therapyVirginia Haurigot, Fátima Bosch|Journal of Clinical Investigation|2013Cited by 231
Long-Term Retinal PEDF Overexpression Prevents Neovascularization in a Murine Adult Model of RetinopathyVirginia Haurigot, Fátima Bosch|PLoS ONE|2012Cited by 75
Progressive neurologic and somatic disease in a novel mouse model of human mucopolysaccharidosis type IIICSara Marcó, Fátima Bosch|Disease Models & Mechanisms|2016Cited by 27