Molecular Trojan Horses for treating lysosomal storage diseasesAndrés Felipe Leal, Shunji Tomatsu, Betül Çelik et al.|Molecular Genetics and Metabolism|2023Cited by 7
Yeast-Produced Human Recombinant Lysosomal β-Hexosaminidase Efficiently Rescues GM2 Ganglioside Accumulation in Tay–Sachs DiseaseOrhan Kerim İnci, Volkan Seyrantepe, Diego A. Súarez et al.|Journal of Personalized Medicine|2025Cited by 1
Human Recombinant Lysosomal β-Hexosaminidase A produced in P.pastoris efficiently reduced GM2 ganglioside accumulation in Tay- Sachs DiseaseOrhan Kerim İnci, Volkan Seyrantepe, Diego A. Súarez et al.|Research Square|2024Cited by 0
Intracerebroventricular Administration of Yeast-Produced Human Recombinant Lysosomal β-Hexosaminidase Partially Corrects GM2 Ganglioside Accumulation in the Tay-Sachs Mouse ModelCarlos Javier Alméciga-Díaz, Angela Johana Espejo-Mojica, Volkan Seyrantepe et al.|İYTE (İZMİR YÜKSEK TEKNOLOJİ ENSTİTÜSÜ)|2025Cited by 0