Genome-scale in vivo CRISPR screen identifies RNLS as a target for beta cell protection in type 1 diabetesErica P. Cai, Yi Peng, Wei Zhang et al.|Nature Metabolism|2020Cited by 98
Direct delivery of Cas-embedded cytosine base editors as ribonucleoprotein complexes for efficient and accurate editing of clinically relevant targetsJeong Min Lee, Celia A. Schiffer|Nucleic Acids Research|2024Cited by 4