Sickle cell disease landscape and challenges in the EU: the ERN-EuroBloodNet perspectiveMaría Del Mar Mañú Pereira, Béatrice Gulbis, Celeste Bento et al.|The Lancet Haematology|2023Cited by 34
Successes and pitfalls in orphan drug development for sickle cell diseaseEnrico Costa, Lucia De Franceschi, Antonella Isgrò et al.|Blood Advances|2024Cited by 16