Successes and pitfalls in orphan drug development for sickle cell diseaseEnrico Costa, Lucia De Franceschi, Mariane de Montalembert et al.|Blood Advances|2024Cited by 16
Addressing global regulatory challenges in rare disease drug developmentEnrico Costa, Steffen Thirstrup, Riccardo Luigetti et al.|Drug Discovery Today|2025Cited by 8
L’accesso ai farmaci per malattie rare tra aspetti regolatori e priorità di salute pubblicaEnrico Costa, Armando A. Genazzani, Gianluca Grimaldi et al.|Recenti Progressi in Medicina|2022Cited by 1